Hematologist/oncologist Elliott Vichinsky, MD, is interviewed by KGO-TV about a new international clinical trial for treatment of a neurdegenerative disease that has already shown promising results in two of his patients. Watch the video report >
"A Chance at Normal Life for Children with Rare Diseases"
(CTSI News © 4/9/2012)
Clinical trials run by gastroenterologist Paul Harmatz, MD, and for children with rare genetic disease MPS. MPS stunts growth, limits movement, and causes severe airway problems that can lead to early death in children. Dr. Harmatz, in collaboration with CTSI at UCSF and BioMarin Pharmaceutical Inc., is conducting 7 MPS-related clinical trials with patients from all over the world
"Clinical Trials of NBIA for Deferiprone to Start"
(KGO-TV, San Francisco, CA © 3/20/2012)
Children's is the US site for an international clinical trial to treat NBIA, a dangerous iron accumulation in the brain. After winning FDA approval for compassionate use to treat two patients suffering from the rare neurodegenerative disorder with a drug called deferiprone, Elliott Vichinsky, MD, documented the success of the drug and is looking forward to the international collaboration.
Going Bald for Kids' Cancer
(NBC Bay Area/KNTV © 3/17/2012)
Coverage of the 2012 Children's St. Baldrick's head shaving fundraiser, including an interview with pediatric oncologist Caroline Hastings, MD.
Shaving Heads for Childhood Cancer Research
(KTVU, Oakland, CA © 3/17/2012)
Leukemia patient Kate and her father talk about participating in Children's St. Baldrick's head shaving event and the importance of funding pediatric cancer research.
"At Children's Hospital Oakland, the Brave Go Bald for Childhood Cancer Research"
(Oakland North © 3/16/2012)
More than 200 men, woman, and children went bald to raise honor kids with cancer and raise money to support pediatric cancer research at Children's 5th annual St. Baldrick's head shaving event. Among the brave women was Irma whose son Ricky just received a bone marrow transplant for leukemia. Pediatric oncologist Caroline Hastings, MD, is also featured in the story.
"Swim Across America Checks Fund Local Cancer Research"
(Berkeleyside © 3/14/2012)
CHORI cancer research scientist Julie Saba, MD, PhD, accepted a $110,000 check for research from Swim Across America's 2011 San Francisco Bay Swim. The donation will be support research condcuted by Bruce Ames, PhD, and skin cancer research led by scientist Ervin Epstein, MD.
"Parents of Twins with Rare Disease Fight for FDA Approval of Treatment"
(USA Today © 3/6/2012)
Children's oncologist Caroline Hastings, MD, secured groundbreaking FDA approval to treat twins with Niemann Pick Type C (known as "childhood Alzheimer's") with a sugar compound called cyclodextrin. The treatment has been promising, but Dr. Hastings and the twins' devoted parents Chris and Hugh Hempel are petitioning for further FDA approval to deliver the drug directly into the brain for even better results.